Sarepta shares fall 37% as FDA questions future of key gene therapy
Friday, 18 July 2025 () Shares of Sarepta Therapeutics fell close to 37% on Friday after reports emerged that the US Food and Drug Administration is considering whether to halt the distribution of Elevidys, the company’s flagship gene therapy for Duchenne Muscular Dystrophy (DMD). The move comes amid an ongoing investigation into multiple patient deaths tied to Sarepta’s gene therapy […]
WASHINGTON, DC—June 4, 2025—Media and the public are invited to listen to the FDA’s Center for Biologics Evaluation and Research (CBER) Cell and Gene Therapy (CGT) Roundtable. This event will..
A child with hereditary deafness regained their hearing thanks to a successful gene therapy surgery. 11-year-old Aissam Dam became the first person to get gene therapy in the United States for..