UK first to OK gene therapy for sickle cell & thalassemia
Friday, 17 November 2023 The UK's medicines regulator has granted approval for the world's first gene therapy treatment for sickle cell disease. The treatment, called Casgevy, is the first medicine to be licensed using the gene editing tool CRISPR. It works by targeting the problematic gene in a patient's bone marrow stem cells, allowing the body to produce properly functioning hemoglobin. Casgevy is currently being reviewed by the US Food and Drug Administration for approval. The makers of the treatment, Vertex Pharmaceuticals and CRISPR Therapeutics, are working with health authorities to establish a price and secure reimbursement for eligible patients.
Gene-Editing, Sickle Cell Treatment , Gets UK Approval .
Regulators in the United Kingdom have
authorized the world's first gene therapy
treatment for people with sickle cell disease.
Regulators in the United Kingdom have
authorized the world's first gene therapy
treatment for people with...
Lots to talk about today - J6, elections, general stupidity - but we are finding new and profound information about the food supply. It was odd that there was so much opposition to HB1169 in Missouri -..
Friday, 17 November 2023
![mRNA in Food - It's Worse Than We Knew [Video]](https://video.newsserve.net/300/v/20231124/1700850209-mRNA-in-Food-It-apos-Worse.jpg)
